This funding supports efficient and innovative natural history studies that generate high-quality, interpretable data to address critical knowledge gaps in rare diseases. The goal is to remove barriers and exert significant impact on specific or multiple rare diseases with similar pathophysiology, thereby facilitating medical product development. The opportunity is open to a broad range of domestic and foreign organizations, including higher education institutions, nonprofits, for-profits, and government entities.
Eligible applicants include a wide range of organizations such as higher education institutions, nonprofits, for-profit organizations, government entities, tribal governments, and foreign organizations. Both domestic and non-domestic entities may apply, including foreign components of U.S. organizat
